No abstract available
Keywords:
oligonucleotide; regulatory; splicing modulation; therapy.
MeSH terms
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Adolescent
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Child
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Clinical Trials as Topic
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Dose-Response Relationship, Drug
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Drug Approval*
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Dystrophin / genetics
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Exons
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Humans
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Morpholinos / therapeutic use*
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Muscular Dystrophy, Duchenne / drug therapy*
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Muscular Dystrophy, Duchenne / economics
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Oligonucleotides / therapeutic use
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Time Factors
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Treatment Outcome
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United States
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United States Food and Drug Administration
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Walk Test
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Young Adult
Substances
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Dystrophin
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Morpholinos
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Oligonucleotides
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PRO051
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eteplirsen